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CN1699 Our Business - Guide for Agents
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1391
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6165
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355
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111
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7954
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33458
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9716
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Development of KoRV-pseudotyped lentiviral vectors for efficient gene transfer into freshly isolated immune cells
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A multinational survey of potential participant perspectives on ocular gene therapy
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Adeno-associated virus genome quantification with amplification-free CRISPR-Cas12a
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Precision ophthalmology: a call for Africa not to be left in the dark
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Advancing rare disease treatment: EMA’s decade-long insights into engineered adoptive cell therapy for rare cancers and orphan designation
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A shedding analysis after AAV8 CNS injection revealed fragmented viral DNA without evidence of functional AAV particles in mice
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Are genetically modified protozoa eligible for ATMP status? Concerning the legal categorization of an oncolytic protozoan drug candidate
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Analytical characterization of full, intermediate, and empty AAV capsids
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Multicenter assessment and longitudinal study of the prevalence of antibodies and related adaptive immune responses to AAV in adult males with hemophilia
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Gene therapy corrects the neurological deficits of mice with sialidosis
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Correction: Cost of gene therapy
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Modeling Glutaric Aciduria Type I in human neuroblastoma cells recapitulates neuronal damage that can be rescued by gene replacement
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