Paediatric clinical study of 3D printed personalised medicines for rare metabolic disorders

Keywords

Semi-solid extrusion 3D printing

Pediatrics

Direct ink writing

Polypills

Patient acceptability of formulations

Additive manufacturing of drug products

Precision pharmaceuticals and drug delivery systems

Abbreviations3DP

Three-dimensional printing

ECHS1

Short-chain Enoyl-CoA Hydratase

FDA

Food and Drug Administration

MHRA

Medicines and Healthcare products Regulatory Agency

MSUD

Maple Syrup Urine Disease

OTC

Ornithine Transcarbamylase

IEC

Ion-exchange chromatography

Data availability

Data will be made available on request.

© 2024 The Author(s). Published by Elsevier B.V.

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