Quantifying the Burden of Hyperphagia in Prader-Willi Syndrome Using Quality-Adjusted Life-years

EQ-5D for the assessment of health-related quality of life and resource allocation in children: a systematic methodological review.

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Applying stated-preference methods to improve health systems in sub-Saharan Africa: a systematic review.

Expert review of pharmacoeconomics & outcomes research. 17: 441-458Beckham SW Crossnohere NL Gross M Bridges JF.

Eliciting Preferences for HIV Prevention Technologies: A Systematic Review.

The Patient-Patient-Centered Outcomes Research. : 1-24Ozawa S Wonodi C Babalola O Ismail T Bridges J.

Using best-worst scaling to rank factors affecting vaccination demand in northern Nigeria.

Vaccine. 35: 6429-6437Ozawa S Grewal S Bridges JF.

Household size and the decision to purchase health insurance in Cambodia: results of a discrete-choice experiment with scale adjustment.

Applied health economics and health policy. 14: 195-204Hashim H Beusterien K Bridges JF Amos K Cardozo L.

Patient preferences for treating refractory overactive bladder in the UK.

International urology and nephrology. 47: 1619-1627Bridges JF Selck FW Gray GE McIntyre JA Martinson NA.

Condom avoidance and determinants of demand for male circumcision in Johannesburg, South Africa.

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Mind the (inter-rater) gap. An investigation of self-reported versus proxy-reported assessments in the derivation of childhood utility values for economic evaluation: A systematic review.

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Is It Time To Take a Harder Look at the QALY?.

Biotechnol Healthc. 5: 47-48Crossnohere NL Fischer R Lloyd A Prosser LA Bridges JFP.

Assessing the Appropriateness of the EQ-5D for Duchenne Muscular Dystrophy: A Patient-Centered Study.

Medical decision making: an international journal of the Society for Medical Decision Making. 41: 209-221Efthymiadou O Mossman J Kanavos P.

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Health Policy. 123: 159-165Patient-Focused Drug Development Draft Guidance: Methods to Identify What is Important to Patients

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Maximum acceptale risk: Alternative measures for quantifying patients’ tolerance for theraputic benefit. International Society for Pharmacoeconomics and Outcomes Research.

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Caregiver priorities for endpoints to evaluate treatments for Prader-Willi syndrome: a best-worst scaling.

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Current and emerging therapies for managing hyperphagia and obesity in Prader-Willi syndrome: A narrative review.

Obes Rev. 21: e12992Fehnel SE Brown TM Nelson L et al.

Development of the Hyperphagia Questionnaire for Use in Prader-Willi Syndrome Clinical Trials.

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Assessment of hyperphagia in Prader-Willi syndrome.

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The disability paradox: high quality of life against all odds.

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Health utilities and parental quality of life effects for three rare conditions tested in newborns.

J Patient-Reported Outcomes. 3: 4Pyne JM Fortney JC Tripathi S Feeny D Ubel P Brazier J.

How bad is depression? Preference score estimates from depressed patients and the general population.

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Can patients diagnosed with schizophrenia complete choice-based conjoint analysis tasks?.

The Patient: Patient-Centered Outcomes Research. 4: 267-275

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J Intern Med. 260: 1-10Hollin IL Young C Hanson C Bridges JF Peay H.

Developing a patient-centered benefit-risk survey: a community-engaged process.

Value Health. 19: 751-757Miller JL Lynn CH Driscoll DC et al.

Nutritional phases in Prader-Willi syndrome.

Am J Med Genet. Part A. 155a: 1040-1049Tsai JH Janssen E Bridges JF.

Research as an event: a novel approach to promote patient-focused drug development.

Patient Preference Adherence. 12: 673-679

Models for count data with overdispersion.

Princeton. Hanley JA Negassa A Edwardes MDd Forrester JE.

Statistical analysis of correlated data using generalized estimating equations: an orientation.

Am J Epidemiol. 157: 364-375Bridges JF Tsai J-H Janssen E Crossnohere NL Fischer R Peay H.

How do members of the Duchenne and Becker muscular dystrophy community perceive a discrete-choice experiment incorporating uncertain treatment benefit? An application of research as an event.

Patient-Centered Outcomes Res. 12: 247-257Patient Preference Information–Voluntary Submission, Review in Premarket Approval Applications, Humanitarian Device Exemption Applications, and De Novo Requests, and Inclusion in Decision Summaries and Device Labeling

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Aging, natural death, and the compression of morbidity.

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Impact of caregiver and parenting status on time trade-off and standard gamble utility scores for health state descriptions.

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Economic burden and health-related quality of life associated with Prader-Willi syndrome in France.

J Intellectual Disabil Res. 60: 879-890Lopez-Bastida J Linertova R Oliva-Moreno J et al.

Social/economic costs and health-related quality of life in patients with Prader-Willi syndrome in Europe.

Eur J Health Econ. 17: 99-108

How Should We Measure Quality of Life Impact in Rare Disease? Recent Learnings in Spinal Muscular Atrophy: Office of Health Economics.

EuroQol–a new facility for the measurement of health-related quality of life.

Health Policy. 16: 199-208

Improving decision analyses: parent preferences (utility values) for pediatric health outcomes.

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Estimation of utilities in attention-deficit hyperactivity disorder for economic evaluations.

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Measuring health preferences for use in cost-utility and cost-benefit analyses of interventions in children.

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Parent Preferences for Health Outcomes Associated with Autism Spectrum Disorders.

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A comparative study of European rare disease and orphan drug markets.

Health Policy. 97: 173-179Crossnohere NL Fischer R Crossley E Vroom E Bridges JF.

The evolution of patient-focused drug development and Duchenne muscular dystrophy.

Expert Rev Pharmacoecon Outcomes Res. 20: 57-68

Post-marketing access to orphan drugs: a critical analysis of health technology assessment and reimbursement decision-making considerations.

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Does mode of administration matter? Comparison of online and face-to-face administration of a time trade-off task.

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Are QALYs based on time trade-off comparable? A systematic review of TTO methodologies.

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