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Available online 9 March 2023
Author links open overlay panelSection snippetsDisclosure of interestM. Anheim declares consultancy honoraria from Teva, Merz, Orkyn, AbbVie, Asdia, Ever Pharma, Reata, Ipsen Pharma.
Reference (1)D. Pellerin et al.Deep intronic FGF14 GAA repeat expansion in late-onset cerebellar ataxiaN Engl J Med
(2023)
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